Company Overview and News

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PTC Therapeutics to Buy Agilis Biotherapeutics in Deal that Could Exceed $945 Million

2018-07-20 biospace
PTC Therapeutics is buying Agilis Biotherapeutics in a deal that has the potential to exceed $945 million with a priority review voucher thrown into the mix as well.
JAZZ PTCT UTHR ONCE

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Pharma Stock Roundup: JNJ & NVS' Q2 Earnings, FDA Approvals

2018-07-20 zacks
J&J (JNJ - Free Report) and Novartis (NVS - Free Report) ringed in the earnings season for the pharma space. Meanwhile, Pfizer (PFE - Free Report) and Lilly’s (LLY - Free Report) pain drug showed early positive results in a late-stage study. The FDA approved J&J’s latest HIV medicine Symtuza as well as label expansion of Pfizer’s prostate cancer drug Xtandi. In the wake of deeper political scrutiny over the high cost of prescription medicines, Novartis said it won’t raise U.
KDP NVS ABBV PFE ABBV ONCE

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Fortress Biotech: A Differentiated Grower Brewing Strong Subsidiaries

2018-07-20 seekingalpha
Fortress is building an impregnable moat by brewing a vast number of subsidiaries that focus on different market niches. Journey Medical subsidiary is providing an increasingly meaningful revenue stream.
MBIO ATXI NHLD FBIO ONCE

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Novartis' (NVS) Kisqali Gets FDA Nod for Label Expansion

2018-07-19 zacks
Novartis AG (NVS - Free Report) announced that the FDA has expanded oncology drug Kisqali’s label.
WFC WFCNP WFC.WS UNP WFC.PRL WFC.PRJ GSK ONCE WFC.PRT WFC.PRR WFC.PRQ WFC.PRP WFC.PRO WFC.PRN NVS GSK WFC.PRY WFC.PRX WFC.PRW WFC.PRV

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Novartis Q2 Earnings Miss, Sales Top on Cosentyx, Entresto

2018-07-18 zacks
Swiss pharma giant Novartis AG (NVS - Free Report) reported results for second-quarter 2018, wherein revenues beat estimate, driven by strong performance of Cosentyx and Entresto. However, earnings fell short.
AMGN NVS ONCE

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Pfizer's Hemophilia B Gene Therapy Candidate Enters Phase III

2018-07-17 zacks
Pfizer Inc. (PFE - Free Report) announced that it initiated a phase III, lead-in study of an experimental gene therapy treatment, fidanacogene elaparvovec, for patients with hemophilia B. Fidanacogene elaparvovec, a high-activity human coagulation factor IX gene, is a one-time treatment option.
HD PFZ 500680 PFE PFIZER ONCE BMRN

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Is a Surprise in the Cards for Novartis in Q2 Earnings?

2018-07-16 zacks
Swiss pharma-giant Novartis AG (NVS - Free Report) is scheduled to report second-quarter 2018 results on Jul 18.
AMGN POOL GTT NVS GSK GSK ONCE

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Rounds Report: Nephros Posts Strong Preliminary Financial Results For Q2

2018-07-13 seekingalpha
The overall bioscience market traded with a mixed sentiment for the day. Nevertheless, many equities under over coverage continued to rally.
NTLA SLDB SGMO CRSP ABEO XBI ONCE RGNX NEPH EDIT ADVM IBB ABEOW

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FDA Releases Additional Framework for Development, Review and Approval of Gene Therapies

2018-07-12 biospace
In mid-December 2017, the U.S. Food and Drug Administration (FDA) released a guidance framework for how researchers should approach gene therapy, in terms of development and regulatory approval. This was initiated on the first-ever approval of a gene therapy for a disease caused by mutations in a specific gene. The therapy was for Spark Therapeutics’ Luxturna (voretigene neparvovec-rzyl) to treat an inherited retinal disease caused by mutations to both copies of the RPE65 gene.
ONCE

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3 Gene Therapy Stocks Investors Can Bet on in Rest of 2018

2018-07-12 zacks
Innovation holds the key in the pharma/biotech sector and most companies have been diverting their resources to develop gene therapy candidates in their goal of finding a cure for difficult and incurable diseases. In the first half of 2018, most pharma/biotech bigwigs and also a number of smaller companies scurried for a lucrative catch in the space either through licensing deals or acquisitions.
BOLD VYGR BLT SLDB ADI NVS BNTC BNIKF PFE ONCE AXON BNTCW

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Axovant Licenses Benitec Gene Therapy Candidates for OPMD, Neurological Disorders

2018-07-09 genengnews
Benitec Biopharma could generate up to $655 million-plus in payments from licensing its preclinical gene therapy for oculopharyngeal muscular dystrophy (OPMD; pictured), and five additional Benitec gene therapy candidates for neurological disorders to to Axovant Sciences. [NIH]
BLT OXB BNTC BNIKF OXBDF ONCE BNTCW AXON

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Axonant Showing Signs Of A Comeback As FDA Increases Scrutiny Of Compounding

2018-07-06 seekingalpha
The overall bioscience market traded with a mixed sentiment for the day. Many equities under our coverage continued to log in further profits for investors.
OXB ESPR IBB XBI OXBDF ONCE AXON

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A Look at Hemophilia Drug Prices and the Market

2018-07-03 biospace
Miracles, it seems, have a high price tag. At least, if those miracles are miracle drugs. There’s no doubt that trends in gene therapy and immuno-oncology are producing drugs that are as close to miraculous as we’re likely to get, doing a great job, generally, in beating back diseases that to this point were untreatable or didn’t respond well to other therapies.
SRPT HZNP BMRN ONCE

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Novartis to Spin-Off Alcon as Separate Trading Company

2018-07-02 zacks
Novartis AG (NVS - Free Report) announced that it intends to spinoff its ophthalmology division, Alcon, into a separately-traded standalone company in order to grow as a medicines company solely.
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2018-07-17 - Asif

History and Development of the Company Kitov Pharma was incorporated under the laws of the State of Israel (under a previous name) on August 12, 1968 and its ordinary shares were originally listed for trading on the TASE in 1978. The company's ordinary shares are currently traded on the TASE under the symbol “KTOV”, and its ADSs and its public warrants are traded on NASDAQ under the symbols “KTOV” and “KTOVW”, respectively. In October 2012, the District Court in Lod, Israel approved the creditors arrangement in accordance with Section 350 of the Companies Law in order to effectuate the sale by Kitov Pharma (then known as Mainrom Line Logistics Ltd.) of all its activities, assets, rights, obligations and liabilities to a private company held by its then controlling shareholders, and all rights of Kitov Pharma’s creditors against it were extinguished. The sale was made pursuant to an arrangement between Kitov Pharma and its creditors. Following such sale and a related cash...

ATHX: Athersys Analysis and Research Report

2018-07-17 - Asif

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CYTX: Cytori Therapeutics Analysis and Research Report

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Silicon Investor Message Boards

This table lists all message boards related to ONCE / Spark Therapeutics, Inc. on message board site Silicon Investor.

Bank loans - is there a reason to be concerned? Conceptus (CPTS)
DTCC Concern DTCC Concern
new CA travel approval policy raises concerns Stock u0026 Related Info. Enter here once and be regular!
CONCENTRA MANAGED CARE INC (CCMC) CUBA- HOW TO INVEST ONCE EMBARGO IS LIFTED
Should Gore concede POLL Once In A Lifetime Opportunity!
CUSIP: 84652J103